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Subjects
- United States3
- Anemia, Sickle Cell -- drug therapy1
- Antibodies, Monoclonal1
- Antibodies, Monoclonal -- therapeutic use1
- Cystic Fibrosis -- drug therapy1
- Cystic Fibrosis Transmembrane Conductance Regulator -- drug effects1
- Genetic Therapy1
- Glutamine -- therapeutic use1
- Hemoglobin, Sickle -- antagonists & inhibitors1
- Hemophilia A -- drug therapy1