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2813. Voretigene neparvovec for biallelic RPE65-mediated retinal disease: effectiveness and value : final evidence report

2814. Chimeric antigen receptor T-cell therapy for B-cell cancers: effectiveness and value : final evidence report

2815. Emicizumab for hemophilia A with inhibitors: effectiveness and value : final evidence report

2816. Modulator treatments for cystic fibrosis: effectiveness and value : final evidence report and meeting summary

2817. Calcitonin gene-related peptide (CGRP) inhibitors as preventive treatments for patients with episodic or chronic migraine: effectiveness and value : final evidence report

2818. Elagolix for treating endometriosis: final evidence report

2819. Targeted immunomodulators for the treatment of moderate-to-severe plaque psoriasis: effectiveness and value : condition update : final evidence report

2820. Inotersen and patisiran for hereditary transthyretin amyloidosis: effectiveness and value : final evidence report