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4643. Voretigene neparvovec for biallelic RPE65-mediated retinal disease: effectiveness and value : final evidence report

4644. Chimeric antigen receptor T-cell therapy for B-cell cancers: effectiveness and value : final evidence report

4645. Emicizumab for hemophilia A with inhibitors: effectiveness and value : final evidence report

4646. Modulator treatments for cystic fibrosis: effectiveness and value : final evidence report and meeting summary

4647. Calcitonin gene-related peptide (CGRP) inhibitors as preventive treatments for patients with episodic or chronic migraine: effectiveness and value : final evidence report

4648. Elagolix for treating endometriosis: final evidence report

4649. Targeted immunomodulators for the treatment of moderate-to-severe plaque psoriasis: effectiveness and value : condition update : final evidence report

4650. Inotersen and patisiran for hereditary transthyretin amyloidosis: effectiveness and value : final evidence report